New Gene Therapy for Hereditary Maculopathy

Hope comes from the USA for those suffering from Hereditary Maculopathy such as Leber’s Congenital Amaurosis or Retinitis Pigmentosa in the form associated with mutation of both pairs of the RPE65 gene. The innovative drug for the treatment of these diseases is called Voretigene Neparvovec. It is able to repair the gene responsible for the […]